NHGRI | Technology Transfer

NON-DISRUPTIVE GENE THERAPY FOR THE TREATMENT OF MMA

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Canada
3109114
Filed on 2018-10-30

Targeted Integration Into The Albumin (Alb) Locus As A Treatment For Hereditary Methylmalonic Acidemia (MMA) Caused By Methylmalonyl-coA Mutase (MUT) Deficiency

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Saudi Arabia
521421222
Filed on 2018-10-30

NON-DISRUPTIVE GENE THERAPY FOR THE TREATMENT OF MMA

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Japan
2021-531445
Filed on 2018-10-30

Targeted Integration Into The Albumin (Alb) Locus As A Treatment For Hereditary Methylmalonic Acidemia (MMA) Caused By Methylmalonyl-coA Mutase (MUT) Deficiency

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Brazil
BR112021002332-1
Filed on 2018-10-30

ABERRANT POST-TRANSLATIONAL MODIFICATIONS (PTMS) IN METHYL- AND PROPIONIC ACIDEMIA AND A MUTANT SIRTUIN (SIRT) TO METABOLIZE PTMS

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Patent Cooperation Treaty
PCT/US2021/028228
Filed on 2021-04-20

Targeted Integration Into The Albumin (Alb) Locus As A Treatment For Hereditary Methylmalonic Acidemia (MMA) Caused By Methylmalonyl-coA Mutase (MUT) Deficiency

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US Application 17/267,482
Filed on 2021-02-09

Targeted Integration Into The Albumin (Alb) Locus As A Treatment For Hereditary Methylmalonic Acidemia (MMA) Caused By Methylmalonyl-coA Mutase (MUT) Deficiency

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Israel
280684
Filed on 2018-10-30

NON-DISRUPTIVE GENE THERAPY FOR THE TREATMENT OF MMA

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Mexico
MX/a/2021/001062
Filed on 2018-10-30

NON-DISRUPTIVE GENE THERAPY FOR THE TREATMENT OF MMA

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Australia
2018436152
Filed on 2018-10-30

METHODS AND COMPOSITIONS OF MMA CONSTRUCTS AND VECTORS

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Mexico
MX/A/2021/000638
Filed on 2019-07-16

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