METHOD FOR PRODUCING RETROVIRUS RNA PACKAGING CASSETTES AND AMPLIED IN THE CYTOPLASM BY AUTOCATALYTIC TOGAVIRUS VECTORS
US Application 60/026,666
Filed on 1996-09-25
Filed on 1996-09-25
SEQUENCE MODIFICATION OF OLIGONUCLEOTIDE PRIMERS TO MAINIPULATE NON-TEMPLATED NUCLEOTIDE ADDITION
US Application 60/005,761
Filed on 1995-10-20
Filed on 1995-10-20
IMPROVED GENE THERAPY CONSTRUCTS FOR THE TREATMENT OF PROPIONIC ACIDEMIA CAUSED BY MUTATIONS IN PROPIONYL-COA CARBOXYLASE ALPHA
US Application 18/723,020
Filed on 2024-06-21
Filed on 2024-06-21
IMPROVED GENE THERAPY CONSTRUCTS FOR THE TREATMENT OF PROPIONIC ACIDEMIA CAUSED BY MUTATIONS IN PROPIONYL-COA CARBOXYLASE ALPHA
European Patent
22856962.0
Filed on 2024-06-27
22856962.0
Filed on 2024-06-27
SYNTHETIC MMAB GENES AND AAV VECTORS TO TREAT COBALAMIN B DEFICIENCY
Patent Cooperation Treaty
PCT/US2024/023432
Filed on 2024-04-05
PCT/US2024/023432
Filed on 2024-04-05
NON-DISRUPTIVE GENE THERAPY FOR THE TREATMENT OF MMA
Japan
2024-000692
Filed on 2024-01-05
2024-000692
Filed on 2024-01-05
OLIGONUCLEOTIDE ANALOGUES TARGETING HUMAN LMNA
Australia
2023274161
Filed on 2023-11-30
2023274161
Filed on 2023-11-30
OLIGONUCLEOTIDE ANALOGUES TARGETING HUMAN LMNA
Singapore
10202303471P
Filed on 2023-12-11
10202303471P
Filed on 2023-12-11
HIGH CONCENTRATION METHYLCOBALAMIN OR COMBINATION OF METHYL- AND HYDROXOCOBALAMIN FOR THE TREATMENT OF COBALAMIN C DEFICIENCY DISORDERS
US Application 18/032,132
Filed on 2023-04-14
Filed on 2023-04-14
NOVEL ADENO-ASSOCIATED VIRAL (AAV) VECTORS TO TREAT HEREDITARY METHYLMALONIC ACIDEMIA (MMA) CAUSED BY METHYLMALONYL-COA MUTASE
(MMUT) DEFICIENCY
US Application 18/026,421
Filed on 2023-03-15
Filed on 2023-03-15