SYNTHETIC GENES FOR THE TREATMENT OF PROPIONIC ACIDEMIA CAUSED BY MUTATIONS IN PROPIONYL-COA CARBOLXYLASE ALPHA
European Patent
20743021.6
Filed on 2022-01-18
20743021.6
Filed on 2022-01-18
Novel Adeno-associated Viral (AAV) Vectors To Treat Hereditary Methylmalonic Acidemia (MMA) Caused By Methylmalonyl-coA Mutase (MMUT) Deficiency
Patent Cooperation Treaty
PCT/US2021/050699
Filed on 2021-09-16
PCT/US2021/050699
Filed on 2021-09-16
HIGH CONCENTRATION METHYLCOBALAMIN OR COMBINATION OF METHYL- AND HYDROXOCOBALAMIN FOR THE TREATMENT OF COBALAMIN C DEFICIENCY AND RELATED DISORDERS
Patent Cooperation Treaty
PCT/US2021/054619
Filed on 2021-10-12
PCT/US2021/054619
Filed on 2021-10-12
METHODS AND COMPOSITIONS OF MMA CONSTRUCTS AND VECTORS
Japan
2021-526207
Filed on 2019-07-16
2021-526207
Filed on 2019-07-16
NON-DISRUPTIVE GENE THERAPY FOR THE TREATMENT OF MMA
India
202117007847
Filed on 2018-10-30
202117007847
Filed on 2018-10-30
METHODS AND COMPOSITIONS OF MMA CONSTRUCTS AND VECTORS
India
202117002972
Filed on 2019-07-16
202117002972
Filed on 2019-07-16
METHODS AND COMPOSITIONS OF MMA CONSTRUCTS AND VECTORS
European Patent
19749899.1
Filed on 2019-07-16
19749899.1
Filed on 2019-07-16
METHODS AND COMPOSITIONS OF MMA CONSTRUCTS AND VECTORS
Canada
3106640
Filed on 2019-07-16
3106640
Filed on 2019-07-16
NON-DISRUPTIVE GENE THERAPY FOR THE TREATMENT OF MMA
China
201880098490.X
Filed on 2018-10-30
201880098490.X
Filed on 2018-10-30
NON-DISRUPTIVE GENE THERAPY FOR THE TREATMENT OF MMA
Russia
2021105822
Filed on 2018-10-30
2021105822
Filed on 2018-10-30