LAMP1 THERAPY IN THE TREATMENT OF LYSOSOMAL STORAGE DISORDERS
US Application 63/162,723
Filed on 2021-03-18
Filed on 2021-03-18
METHODS FOR TREATMENT OF SUBJECTS WITH PREEXISTING IMMUNITY TO VIRAL TRANSFER VECTORS
US Application 62/981,564
Filed on 2020-02-26
Filed on 2020-02-26
METHODS FOR TREATMENT OF SUBJECTS WITH PREEXISTING
IMMUNITY TO VIRAL TRANSFER VECTORS
US Application 62/981,555
Filed on 2020-02-26
Filed on 2020-02-26
METHODS FOR TREATMENT OF SUBJECTS WITH PREEXISTING IMMUNITY TO VIRAL TRANSFER VECTORS
US Application 62/924,143
Filed on 2019-10-21
Filed on 2019-10-21
METHODS FOR TREATMENT OF SUBJECTS WITH PREEXISTING IMMUNITY TO VIRAL TRANSFER VECTORS
US Application 62/624,103
Filed on 2019-10-21
Filed on 2019-10-21
METHODS FOR TREATMENT OF SUBJECTS WITH PREEXISTING IMMUNITY
US Application 62/829,771
Filed on 2019-04-28
Filed on 2019-04-28
METHODS AND COMPOSITIONS OF MMA CONSTRUCTS AND VECTORS
US Application 62/839,761
Filed on 2019-04-28
Filed on 2019-04-28
Novel Adeno-associated Viral (AAV) Vectors To Treat Hereditary Methylmalonic Acidemia (MMA) Caused By Methylmalonyl-coA Mutase (MMUT) Deficiency
US Application 63/080,337
Filed on 2020-09-18
Filed on 2020-09-18
METHODS AND COMPOSITIONS OF MMA CONSTRUCTS AND VECTORS
US Application 62/698,528
Filed on 2018-07-16
Filed on 2018-07-16
DIAGNOSIS AND TREATMENT OF VEXAS, WITH MOSAIC MISSENSE MUTATIONS IN UBA1
US Application 63/059,107
Filed on 2020-07-30
Filed on 2020-07-30