Novel Codon-optimized And Tagged Human NPC1 Genes And AAV Vectors For The Treatment Of Niemann-Pick Type C1 Deficiency And Related Conditions
US Application 62/522,677
Filed on 2017-06-20
Filed on 2017-06-20
METHODS OF DETECTING AND TREATING GATM-RELATED RENAL DISORDERS
US Application 62/515,834
Filed on 2017-06-06
Filed on 2017-06-06
CANCER DETECTION AND CLASSIFICATION
US Application 62/898,670
Filed on 2019-09-11
Filed on 2019-09-11
OLIGONUCLEOTIDE ANALOGUES TARGETING HUMAN LMNA
US Application 62/330,027
Filed on 2016-04-29
Filed on 2016-04-29
Gene Therapy For Combined Methylmalonic Acidemia/Aciduria and Hyperhomocysteinemia/Homocystinuria, Cobalamin C Type, and Deficiency of MMACHC
US Application 62/279,285
Filed on 2016-01-15
Filed on 2016-01-15
Gene Therapy For Cobalamin C Deficiency
US Application 62/266,352
Filed on 2015-12-11
Filed on 2015-12-11
New Pan-Cancer Detection Methods
US Application 62/220,041
Filed on 2015-09-17
Filed on 2015-09-17
A Method of Detecting Molecules in Proximity to a Target Molecule in a Sample
US Application 62/211,160
Filed on 2015-08-28
Filed on 2015-08-28
Tagged Form Of Mut Enzyme, Genetic Constructs Incorporating It, And Its Use In Gene Therapy
US Application 62/152,520
Filed on 2015-04-24
Filed on 2015-04-24
Sialylation-increasing Therapies For Diseases Associated With Oxidative Stress
US Application 62/120,742
Filed on 2015-02-25
Filed on 2015-02-25