Compounds and Method for Treating PARP1-Deficient Cancers
US Application 61/930,291
Filed on 2014-01-22
Filed on 2014-01-22
METHODS FOR TREATING LEUKEMIA AND DISORDERS MEDIATED BY MLL FUSION PROTEINS
US Application 61/736,459
Filed on 2012-12-12
Filed on 2012-12-12
Compositions and Methods for Predicting Age of Onset of A Lysosomal Storage Disease or a Disease Associated with a Lysosomal Defect
US Application 61/781,807
Filed on 2013-03-14
Filed on 2013-03-14
Biomarker For Hyposialylation Disorders
US Application 61/785,094
Filed on 2013-03-14
Filed on 2013-03-14
Methods For Treating Progeroid Laminopathies Using Oligonucleotide Analogues Targeting Human Lamin A (LMNA)
US Application 61/568,590
Filed on 2011-12-08
Filed on 2011-12-08
Synthetic Methylmalonyl-CoA Mutase Transgene For The Treatment Of Mut Class Methylmalonic Acidemia (MMA)
US Application 61/792,081
Filed on 2013-03-15
Filed on 2013-03-15
Recurrent Mutation In Mitogen-Activated Protein Kinase Kinase Kinase 5 (MAP3K5) For Diagnosing And Treating Melanoma
US Application 61/708,785
Filed on 2012-10-02
Filed on 2012-10-02
Silent Mutation In Bcl-2-Like Protein 12 (BCL2L12) For Diagnosing and Treating Melanoma
US Application 61/673,454
Filed on 2012-07-19
Filed on 2012-07-19
Encapsulated N-acetyl-mannosamine (ManNAc) And N-acetylneuraminic Acid (NANA Or Neu5Ac) To Increase Sialylation
US Application 61/531,934
Filed on 2011-09-07
Filed on 2011-09-07