IMPROVED GENE THERAPY CONSTRUCTS FOR THE TREATMENT OF PROPIONIC ACIDEMIA CAUSED BY MUTATIONS IN PROPIONYL-COA CARBOXYLASE ALPHA

Technology
E-034-2022
Patent ID
E-034-2022-0-US-02
Country
US
Application Type
National Stage
Patent Status
Pending
Patent Number
 
Publication Number
US-2025-0049952-A1
Application Number
18/723,020
IC
NHGRI
Date Filed
Date Issued
 
Patent PDF