ADENO ASSOCIATED VIRAL (AAV) VECTORS FOR TREATMENT OF PROPIONIC ACIDEMIA (PA) CAUSED BY MUTATIONS IN PROPIONYL-COA CARBOXYLASE BETA (PCCB)
Technology
E-222-2024
Patent ID
E-222-2024-0-PC-01
Country
PCT
Application Type
PCT
Patent Status
Pending
Patent Number
Publication Number
Application Number
PCT/US2025/050511
IC
NHGRI
Date Filed
Date Issued
Patent PDF