ADENO ASSOCIATED VIRAL (AAV) VECTORS FOR TREATMENT OF PROPIONIC ACIDEMIA (PA) CAUSED BY MUTATIONS IN PROPIONYL-COA CARBOXYLASE BETA (PCCB)
Technology
E-222-2024
Patent ID
E-222-2024-0-US-01
Country
US
Application Type
Patent Status
Expired
Patent Number
Publication Number
Application Number
63/706,441
IC
NHGRI
Date Filed
Date Issued
Patent PDF